Autoimmune disease of the liver which causes the destruction of the small bile ducts - liver only
Aetiology
- Autoimmune
- Much more common in women (10:1), especially middle-aged women
Pathophysiology
- 90% of people with PBC have anti-mitochondrial antibodies (AMAs) against pyruvate dehydrogenase complex (PDC-E2) - enzyme complex found in mitochondria
- T cell mediated - CD4+ cells react against antibodies
Clinical presentation
- Usually asymptomatic/incidental finding - most will not develop symptoms, and most will not develop cirrhosis/liver failure
- Symptoms can include:
- Fatigue
- Itch without rash
- Xanthelasma and xanthomas
Investigations
2 of:
- Positive AMA
- Cholestatic LFTs - ALP > ALT/AST, ↑ GGT, ↑ bilirubin
- Liver biopsy
Management
Ursodeoxycholic acid
- First line
- Increases flow of bile to wash the toxic bile salts out
Obeticholic acid
- Second line
- Alters the inflammatory cholesterol metabolism